From the 2018 European Society for Blood and Marrow Transplantation (EBMT) Annual Meeting, held in Lisbon, Portugal, Régis Peffault de Latour, MD, PhD, of Saint Louis Hospital, Paris, France, discusses the treatments currently available for treating paroxysmal nocturnal hemoglobinuria (PNH). He states how classic PNH can be treated effectively with complement blockers, thus transplant tends to not be an option. However, with PNH associated with aplastic anemia, transplantation is the only curative treatment available with minimal toxicities and a successful outcome.
